J Clin Invest. 2026 May 15;136(10):e198519. doi: 10.1172/JCI198519. eCollection 2026 May 15.
ABSTRACT
PB&TURSO was associated with improved or stabilized pancreatic function, vision, and overall symptom burden in individuals with Wolfram syndrome, a rare and progressive degenerative disease.
PMID:42138079 | DOI:10.1172/JCI198519